WILL GENE THERAPY CURE US - genetic diseases documentary

Now researchers can edit the very smallest genetic errors that cause many different diseases in humans. Two new technologies make it possible without cutting and pasting our DNA. Two different research teams from the Cambridge Broad Research Institute, Cambridge, have developed a tool that they hope to use to correct the smallest genetic defects, mutations, related to cancer, diabetes and many other human diseases. "For most of the genetic diseases caused by a single mutation, there is currently no cure. The hope is that in the future we will be able to provide effective and safe treatment that is enough for life. I hope our study will take us one step closer to the goal, "said David Liu, re-researcher behind a new study published in the journal Nature. Slippers cut DNA He and his colleagues are behind a new redevelopment technique that can correct genetic mutations. According to researchers, it should be less risky than the groundbreaking gene crisp CasprCas9, which has made it possible to cut out defective genes that cause disease and replace them with a new functional variant. Gensaxen CrisprCas9 is based on the fact that the cells' own machinery joins the DNA string correctly after it has been cut. But it happens that it goes wrong, causing small errors to sneak in. It has also been difficult to correct the single mutations that are only caused by an incorrect building block in the genes. But with the new editing tool, you no longer need to rely on the cell's own storage system to do the right thing.