This baby just received the world's first CUSTOM CRISPR treatment

Scientists have achieved a medical breakthrough with the world's first personalized gene therapy. This treatment saved K.J. Muldoon from a rare genetic disorder, showcasing a new era in medicine. It's a pivotal moment for science, suggesting a future where treatments are tailored to the individual. ------------------------------------------------------------------------------------------------------------------------------------------- Meet KJ Muldoon. He was born with a rare and life-threatening genetic disorder. But in February 2025, at just 7 months old, KJ received a treatment that was truly unprecedented: the world's first-ever personalized gene therapy. Up until now, medicine has largely been a "one-size-fits-all" approach. Up until now, These treatments often manage the disease well. But they don’t work the same for everyone. The idea of "personalized medicine" – a treatment crafted specifically for your unique genetic blueprint, designed to correct your individual error – has been long sought after but only really found in the pages of scientific and medical journals. Until now. This is the incredible story of Baby K.J., the groundbreaking science that saved him, and the dawn of a new era in medicine. ------------------------------------------------------------------------------------------------------------------------------------------- Chapters: 0:00 Intro 1:09 Baby KJ 2:36 Symptoms, treatments, and complications of CPS1 4:56 CRISPR editing & limitations 6:39 Personalized CRISPR gene therapy with lipid nanoparticles (LNPs) 8:43 Clinical data 10:00 Ethics of CRISPR 11:22 Future perspectives on personalized medicine -------------------------------------------------------------------------------------- Video about KJ that will make you cry:    • A Breakthrough in Medicine: Personalized G...   News article about KJ released by the Children’s Hospital of Philadelphia (written for a non-technical audience): https://www.chop.edu/news/worlds-firs... Full technical article by Dr. Kiran Musunuru and Dr. Rebecca C. Ahrens-Nicklas: https://www.nejm.org/doi/full/10.1056... Video describing lipid nanoparticles (LNPs):    • Brain rot doesn't understand lipid nanopar...   #scienceexplained #crispr #edutainment #medicine #biotechnology #genetherapy #videoessay